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Archive for November, 2014

Nov 14

Thank you PPMD for including our story to the FDA

Parent Project Muscular Dystrophy compiled compelling stories from the Duchenne community and submitted them to the FDA in a paper titled “Patients are Waiting.”  Jackson’s story is included on Pages 14-15.  Thanks PPMD for all you do!  Read the paper here.

Nov 14

Little Hercules Foundation provides funding for gene therapy

The Little Hercules Foundation, a member of the Duchenne Alliance, is proud to have funded Follistatin, a gene therapy that will potentially help ALL boys with Duchenne.  Read the press release here.

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